Lorenzo Dionisio
Martín Fumero
Part Time Assistant Professor (Health Science)
Hospital Infantil Universitario Niño Jesus de Madrid
Madrid, EspañaPublications in collaboration with researchers from Hospital Infantil Universitario Niño Jesus de Madrid (1)
2010
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Clinical experience with miglustat therapy in pediatric patients with Niemann-Pick disease type C: A case series
Molecular Genetics and Metabolism, Vol. 99, Núm. 4, pp. 358-366