Lorenzo Dionisio
Martín Fumero
Profesor Asociado Asistencial
Hospital de Santa Maria
Lisboa, PortugalPublikationen in Zusammenarbeit mit Forschern von Hospital de Santa Maria (1)
2010
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Clinical experience with miglustat therapy in pediatric patients with Niemann-Pick disease type C: A case series
Molecular Genetics and Metabolism, Vol. 99, Núm. 4, pp. 358-366