Instituto Universitario de Tecnologías Biomédicas
Institut de recherche
Novo Nordisk
Copenhagen, DinamarcaPublications en collaboration avec des chercheurs de Novo Nordisk (3)
2017
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siRNA therapeutics to treat liver disorders
Safety and Efficacy of Gene-Based Therapeutics for Inherited Disorders (Springer International Publishing), pp. 159-190
2016
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Inhibition of glycolate oxidase with dicer-substrate siRNA reduces calcium oxalate deposition in a mouse model of primary hyperoxaluria type 1
Molecular Therapy, Vol. 24, Núm. 4, pp. 770-778
2009
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HCLK2 is required for activity of the DNA damage response kinase ATR
Journal of Biological Chemistry, Vol. 284, Núm. 7, pp. 4140-4147