Clinical experience with miglustat therapy in pediatric patients with Niemann-Pick disease type C: A case series
- Pineda, M.
- Perez-Poyato, M.S.
- O'Callaghan, M.
- Vilaseca, M.A.
- Pocovi, M.
- Domingo, R.
- Ruiz Portal, L.
- Verdú Pérez, A.
- Temudo, T.
- Gaspar, A.
- Garcia Peñas, J.J.
- Roldán, S.
- Martín Fumero, L.
- Blanco de la Barca, O.
- García Silva, M.T.
- Macías-Vidal, J.
- Coll, M.J.
ISSN: 1096-7192, 1096-7206
Year of publication: 2010
Volume: 99
Issue: 4
Pages: 358-366
Type: Article